By upregulating the expression of the lone functioning copy of SCN2A, scientists addressed deficient brain signaling and reduced seizures.

Forecasts in biotech market indicate that by 2030, gene therapy will become more accessible, potentially generating hundreds ...

Genetic editing holds promise to treat incurable diseases, but the most popular method—CRISPR—sometimes does more harm than ...

Could CRISPR Fix this Severe Childhood Brain Disorder?A technology that activates healthy genes reduced seizures in a mouse model of a severe genetic ...

This topic explores the application of advanced biotechnological approaches—including genetic engineering tools such as ...

Disease-resistant pigs, faster-growing fish and heat-tolerant cows are among a new class of animals that are being ...

When brain development gets off to a bad start, the consequences are lifelong.   One example is a condition called SCN2A haploinsufficiency, in which children are born with just one functioning copy ...

Stanford Medicine researchers have developed an artificial intelligence tool to help scientists better plan gene-editing ...

Stanford Medicine researchers have developed an artificial intelligence tool to help scientists better plan gene-editing ...

The 2020 Nobel Prize in Chemistry was awarded for the development of CRISPR/Cas9, a method also known as "gene scissors," ...