Patients aged 10-50 are being sought for a clinical trial testing SAR446268, a gene therapy for myotonic dystrophy type 1 ...

A combined regimen of testosterone and growth hormone improves muscle mass, strength, and mobility in men with FSHD, a study ...

People with rare diseases may need additional forms of support, but we all require community and connection, columnist ...

Mallory Dupree hasn't let a Duchenne muscular dystrophy diagnosis keep her from living the life she wants to live.

Alan Chaulet highlights the glaring lack of access to personal finance tools that people with DMD and other disabilities face ...

To live with dignity, columnist Shalom Lin argues, young adults with disabilities in Singapore deserve stronger housing ...

Three scientists who helped lay the groundwork to develop new treatments for DMD have been awarded the 2025 Louisa Gross ...

Finding humor and joy in life might not change your situation, but it can change your perspective on it, columnist Robin ...

Duvyzat's approval stemmed from the Phase 3 EPIDYS clinical trial that tested the therapy against a placebo in 179 boys with ...

Gui Panhota knows that living with Duchenne MD can pose obstacles, but he says always looking for solutions helps him ...

Alan Chaulet is an entrepreneur fighting Duchenne muscular dystrophy from Lexington, Massachusetts. He graduated from Bentley ...

Gui Panhota is an economist working in the financial markets, having worked at Bank of America in Brazil, and also with ...