The 2025 Research Innovation Grants are supporting projects focused on biomarkers, risk factors, and treatments for ALS.

A young boy born with a devastating, rare genetic condition has been given a new lease of life thanks to a team of UCL ...

Oliver's gene therapy was confirmed to be working, with him thriving months after the treatment. Now, his speech, agility, ...

Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...

To discover more about Nature’s Fynd, visit. To learn about their remarkable nutritional fungi protein and fermentation ...

Explore how next-generation analytical methods empower researchers with accurate, consistent AAV titer measurement for gene ...

Mixed headlines have plagued the cell and gene therapy space of late. We believe that a renewed case of optimism is not only ...

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

This academic-industry partnership reflects the need for a multidisciplinary approach to innovation in cell and gene therapy manufacturing.

The CRISPR Cas9 gene editing tool — the genetic scissors that won the 2020 Nobel Prize in Chemistry — is essentially based on ...

Three-year-old Oliver becomes first Hunter syndrome patient to receive gene therapy, showing remarkable progress a year after treatment.